Clinical trials are research studies that test new treatments or therapies to ensure they are safe, effective, and beneficial for patients.
Amálie, Czech Republic
Welcome to our Clinical Trials page
Here, you can find the latest on clinical trials for Leigh’s syndrome, including those that are currently recruiting participants, active but not recruiting, and those recruiting by invitation only. All this information is linked directly to ClinicalTrials.gov, so it’s always up to date. We also give provide information about clinical trials in general and about the FDA.
Clinical trials offer hope and potential breakthroughs in treatment. At the same time, it’s important to consider the possible benefits and risks, the commitment required, and how a trial might align with your or your loved one’s healthcare journey.
Leigh Syndrome Clinical Trials
Information About
Clinical Trials and the FDA
Find a Clinical Trial on ClinicalTrials.gov
ClinicalTrials.gov is a database of privately and publicly funded clinical studies conducted around the world.
Clinical Trials: What Patients Need to Know
Click on the below above to learn more about what clinical trials are, phases of clinical trials, your rights as a participant, and more.
Informed Consent for Clinical Trials
Informed consent means much more than getting research participant’s signature on the consent form. Click link below to learn more.
FDA – All Resources for Patients
Learn about treatments, drug/device approvals, public meetings and more.
FDA Patient Engagement Opportunities
Learn how you as a patient can engage with the FDA and share your experiences, preferences and needs as they relate to FDA-regulated medical products.
Activity book for children
The “Sofia Learns About Research” activity book presents research in a non-threatening way by describing the journey of Sofia, a child with asthma. You are invited to join Sofia as she learns about health research and considers enrolling in a clinical trial.
Sofia as She Learns About Health Research and Considers Enrolling in a Clinical Trial
Clinical Trial Process
Clinical trials ensure treatments are safe and effective. Each phase helps answer a different question about the treatment. The phases can be combined or referred to as early, late, and/or pivotal stages of development.
